Boosting delivery of rare disease therapies: the IRDiRC Orphan Drug Development Guidebook is out!
The IRDiRC new review has been published on Nature Reviews – Drug Discovery. The paper is authored by the Orphan Drug Development Guidebook (ODDG) Task force that has helped reaching the IRDiRC goal 2 ‘1000 new therapies for rare diseases will be approved, the majority of which will focus on diseases without approved options’ by 2027.…